transthyretin amyloidosis

Alnylam, Onpattro, US FDA, FDA advisory committee, transthyretin amyloidosis, ATTR-cardiomyopathy

FDA doubts Onpattroā€™s benefit in heart disease, Alnylam faces Pfizer hurdle

Anika Sharma

The FDA has raised significant concerns about Alnylam’s attempt to expand the use of Onpattro for the treatment of transthyretin ...