BioMarin

BioMarin, Rare disease, pipeline update, Roctavian, gene therapy, hemophilia A, Pipeline addition

BioMarin R&D chief reveals two new pipeline candidates and strategy to sustain innovation

Anika Sharma

BioMarin, the California-based biotech giant, is embarking on a mission to create its most robust pipeline in history, with a ...

Voxzogo Demand Exceeds Supply, BioMarin Faces Growth Limit

Voxzogo Demand Outstrips Supply: BioMarin’s Growth Dilemma

SG Tylor

BioMarin is facing challenges due to the overwhelming success of its drug, Voxzogo, used to treat achondroplasia, a type of ...

BioMarin's Roctavian_ FDA Approves Hemophilia A Gene Therapy with Positive Reception from Physician | pharmtales

BioMarin’s Roctavian: FDA Approves Hemophilia A Gene Therapy with Positive Reception from Physician

SG Tylor

Source – BioMarin BioMarin’s Roctavian, a gene therapy for severe hemophilia A, has received FDA approval after initial rejection in ...

Analysts predict that BioMarin's hemophilia gene therapy may succeed in Europe

Analysts predict that BioMarin’s hemophilia A gene therapy may succeed in Europe

SG Tylor

According to a report published by SVB Securities analysts Joseph Schwartz and Joori Park, Ph.D., Roctavian may have a “significant ...