You Won’t Believe How Much These 10 Drugs Cost! 😱

~ $3.9 million

Libmeldy

World’s Costliest Drug Libmeldy for the Treatment of Rare Disease MLD

~ $3.6 million

Upstaza

A Life-Changing Gene Therapy for Severe Aromatic L-Amino Acid Decarboxylase Deficiency.

~ $3.5 million

Hemgenix

A one-time gene therapy for the treatment of adults with hemophilia B

~ $3 million

Skysona

A personalized gene therapy to treat boys 4-17 years of age with early, active cerebral adrenoleukodystrophy (CALD)

~ $2.8 million

Zynteglo

Gene therapy for beta-thalassemia using patient’s own cells with beta-globin gene.

~ $2.1 million

Zolgensma

ZOLGENSMA is a prescribed gene therapy indicated for the treatment of spinal muscular atrophy (SMA) in children under the age of 2.

~ $1 million

Danyelza

Treating high-risk neuroblastoma in children (≥1 year) and adults with relapsed or refractory cases.

~ $975,520

Kimmtrak

Prescribed for HLA-A*02:01–positive adults with unresectable or metastatic uveal melanoma, an aggressive form of eye cancer.

~ $929,951

Myalept

Prescribed medication that replenishes the vital hormone leptin, addressing its deficiency in individuals with generalized lipodystrophy (GL).

~ $850,000

Luxturna

Luxturna is a medicine that is used to treat inherited retinal dystrophy, a rare genetic disorder.

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